In Crowded Market for a Rare Disease, Ionis Bets Patients Will Switch to Its New First-in-Class Drug
As with most rare diseases, the market for hereditary angioedema drugs is small. It’s also relatively crowded, served by several ...
Tag: Rare
FDA Turns Down Capricor Cell Therapy for Cardio Complications of Rare Muscle Disease
Capricor Therapeutics’ cell therapy for Duchenne muscular dystrophy has come up short at the FDA, with the regulator rejecting the ...
At ASCO, Merck KGaA Shows How Its Drug Measures Up as Treatment for Rare Type of Tumor
Patients with tenosynovial giant cell tumor can take some comfort in knowing that this rare type of tumor affecting joints ...
Illumina’s PromoterAI unlocks rare disease clues in noncoding genome
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Late abortions are rare. The US just lost a clinic that offered the procedure for over 50 years
Mementos are placed at a memorial outside Women's Health Care Services owned by Dr. George Tiller in Wichita, Kan., Tuesday, ...
Accelerated FDA Approval Makes Verastem Drug the First Therapy for Rare Type of Ovarian Cancer
A rare type of ovarian cancer that grows slowly and responds poorly to chemotherapy now has its first FDA-approved treatment, ...
The Rare Surgery That Saved Their Lives
Born twice? It sounds impossible, but that's exactly the story of miracle baby Rafferty Isaac in the U.K. At just ...
Man Dies From Rare Infection After Dog Licks Wound; Coroner Issues Warning
A 49-year-old man from Ireland, described by relatives as "fit as a fiddle," tragically died from a rare infection that ...
Low doses of antibiotic work just as well as higher ones to treat rare type of chronic hair loss, study finds
Credit: Unsplash/CC0 Public Domain Small amounts of a common antibiotic and anti-inflammatory drug can curb symptoms where a misplaced immune ...
Beam Base Editor’s Early Data in Rare Liver Disease Tee Up $500M Stock Sale in Tough Market
A Beam Therapeutics gene-editing therapy designed to fix a mutation at the root of a rare liver protein deficiency now ...
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